No abstract available
MeSH terms
-
Adolescent
-
Child
-
Clinical Trials as Topic
-
Gene Deletion
-
Humans
-
Male
-
Morpholinos / administration & dosage
-
Morpholinos / pharmacology*
-
Muscular Dystrophy, Duchenne / drug therapy*
-
Oligonucleotides, Antisense*
Substances
-
Morpholinos
-
Oligonucleotides, Antisense
-
eteplirsen