Cutaneous manifestations of immune dysregulation, polyendocrinopathy, enteropathy, X-linked (IPEX) syndrome

Br J Dermatol. 2009 Mar;160(3):645-51. doi: 10.1111/j.1365-2133.2008.08835.x. Epub 2008 Sep 15.

Abstract

Background: Immune dysregulation, polyendocrinopathy, enteropathy, X-linked (IPEX) syndrome is a rare disorder characterized by neonatal autoimmune enteropathy, diabetes and thyroiditis, food allergies and skin rash. IPEX syndrome is caused by mutations in FOXP3, a master control gene of regulatory T cells (Tregs), resulting in absent or dysfunctional Tregs. Data in the literature are scarce and the cutaneous manifestations are rarely depicted.

Objectives: To evaluate the frequency and characteristics of cutaneous manifestations found in IPEX.

Methods: Retrospective single-centre study of a case series of IPEX. Patients' data were retrieved from medical files and numerous parameters concerning general and cutaneous characteristics of the disease were recorded.

Results: Ten children with IPEX were studied. Cutaneous involvement was present in seven of 10 children; age at onset was 0-4 months, median 1.5. All patients presented with atopic dermatitis (AD). Three presented more psoriasiform lesions. Eczema was severe; most affected areas were lower limbs, trunk and face. Pruritus was present in four of seven, and painful fissurary cheilitis in four of seven. Hyper-IgE was found in seven of 10 and hypereosinophilia in five of 10. Skin biopsies showed eczematiform or psoriasiform features. Affected patients were improved by dermocorticoids; no clear improvement was obtained with immunosuppressive regimens. Other features were urticaria secondary to food allergies and staphylococcal sepsis, mostly Staphylococcus aureus and catheter related.

Conclusions: AD seems to be a frequent finding in IPEX syndrome, which is characterized by Treg anomalies. This hints to a possible role of Tregs in AD, which is then discussed in this study.

MeSH terms

  • Biopsy
  • Dermatitis, Atopic / drug therapy
  • Dermatitis, Atopic / genetics
  • Dermatitis, Atopic / pathology
  • Diarrhea, Infantile / genetics
  • Forkhead Transcription Factors / genetics
  • Genetic Diseases, X-Linked / drug therapy
  • Genetic Diseases, X-Linked / genetics
  • Genetic Diseases, X-Linked / pathology*
  • Glucocorticoids / therapeutic use
  • Humans
  • Infant
  • Infant, Newborn
  • Male
  • Mutation
  • Polyendocrinopathies, Autoimmune / drug therapy
  • Polyendocrinopathies, Autoimmune / genetics
  • Polyendocrinopathies, Autoimmune / pathology*
  • Retrospective Studies
  • Skin / pathology
  • Skin Diseases, Genetic / drug therapy
  • Skin Diseases, Genetic / genetics
  • Skin Diseases, Genetic / pathology*
  • Syndrome

Substances

  • FOXP3 protein, human
  • Forkhead Transcription Factors
  • Glucocorticoids