Molecular Therapy
Volume 8, Issue 3, September 2003, Pages 495-500
ArticleMinicircle DNA vectors devoid of bacterial DNA result in persistent and high-level transgene expression in vivo
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Keywords
minicircle
φC31 integrase
linear DNA
expression cassette
bacterial backbone
transgene
human α1-antitrypsin
human factor IX
transcriptional silencing
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Copyright © 2003 The American Society of Gene Therapy. Published by Elsevier Inc. All rights reserved.