Molecular Therapy
Volume 2, Issue 3, September 2000, Pages 256-261
ArticleProlonged Correction of Hyperlipidemia in Mice with Familial Hypercholesterolemia Using an Adeno-Associated Viral Vector Expressing Very-Low-Density Lipoprotein Receptor
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Key Words
gene therapy
liver
cellular immunity
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Abbreviations used: FH, familial hypercholesterolemia; AAV, adeno-associated virus; VLDL, very low-density lipoproteins; LDL, low-density lipoproteins: IDL, intermediate density lipoproteins.
Copyright © 2000 American Society for Gene Therapy. Published by Elsevier Inc. All rights reserved.