agalsidase alfa

Agalsidase alfa versus agalsidase beta for the treatment of Fabry disease: an international cohort study
Maarten Arends, Marieke Biegstraaten, Christoph Wanner, Sandra Sirrs, Atul Mehta, Perry M Elliott, Daniel Oder, Oliver T Watkinson, Daniel G Bichet, Aneal Khan, Mark Iwanochko, Frédéric M Vaz, André B P van Kuilenburg, Michael L West, Derralynn A Hughes, Carla E M Hollak

Journal of Medical Genetics May 2018, 55 (5) 351-358; DOI: 10.1136/jmedgenet-2017-104863

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agalsidase alfa