Table 1

Demographics of patients with MPS VII (n=56)

StatisticsValue
Number enrolledn56
Gender
 Male30 (53%)
 Female20 (36%)
 Unknown*6 (11%)
Ethnicity
 Caucasian—Non-Hispanicn (%)35 (62%)
 Caucasian—Hispanicn (%)10 (18%)
 Black or African-Americann (%)5 (9%)
 Asiann (%)4 (7%)
 Native Hawaiian or other Pacific Islandern (%)1 (2%)
 Othern (%)1 (2%)
Country
 Braziln (%)15 (27%)
 USAn (%)11 (20%)
 Germanyn (%)10 (18%)
 Argentinan (%)6 (11%)
 Spainn (%)4 (7%)
 Turkeyn (%)3 (5%)
 Japann (%)2 (3%)
 Malaysian (%)2 (3%)
 Mexicon (%)1 (2%)
 Australian (%)1 (2%)
 Lithuanian (%)1 (2%)
Age at the last visit to the physician
Min0.3
Max30
Mean13.25
Median11
Range29.7
Kurtosis−1.11
Status at time of interview
 Livingn (%)30 (53%)
 Deceasedn (%)20 (36%)
 Unknown†n (%)6 (11%)
  • *Gender unknown: diagnosed in utero, sex undetermined.

  • †Status at the time of interview: lost to follow-up.

  • MPS VII, mucopolysaccharidosis VII.